Search Results 1-10 of 15750 for Duchenne+muscular+dystrophy

  1. Mayo Clinic Q and A: Understanding Duchenne muscular dystrophy

    Currently, there is no cure. Muscular dystrophy is an umbrella term applied to a group of muscle diseases in which there is a known genetic abnormality that ...

  2. Muscular dystrophy - Symptoms & causes - Mayo Clinic

    Muscle pain and stiffness; Learning disabilities; Delayed growth. Becker muscular dystrophy. Signs and symptoms are similar to those of Duchenne muscular ...

  3. Muscular dystrophy - Diagnosis & treatment - Mayo Clinic

    In 2019, the Food and Drug Administration (FDA) approved golodirsen (Vyondys 53) for treatment of some people with Duchenne dystrophy who have a certain genetic ...

  4. Viltolarsen (Intravenous Route) Description and Brand Names - Mayo Clinic

    Viltolarsen injection is used to treat Duchenne muscular dystrophy (DMD) in patients with a confirmed specific genetic mutation. DMD is a rare, inherited muscle ...

  5. Deflazacort Expanded Access Program for Children, Adolescents and Adults With Duchenne Muscular Dystrophy - Mayo Clinic

    About this study. The expanded access program will provide access to treatment with deflazacort in children, adolescent, and adult patients with DMD in the ...

  6. Muscular dystrophy - Doctors and departments - Mayo Clinic

    ... Duchenne muscular dystrophy, Degenerative disk disease, Cervical spondylotic myelopathy, Arthropathy, Inflammatory arthritis, Radiculopathy, Muscle weakness ...

  7. Deflazacort (Oral Route) Description and Brand Names - Mayo Clinic

    Deflazacort is used to treat Duchenne muscular dystrophy (DMD). DMD is a rare, inherited muscle disease that occurs usually in children and young adults and ...

  8. Delandistrogene Moxeparvovec-Rokl (Intravenous Route) Description and Brand Names - Mayo Clinic

    ... Duchenne muscular dystrophy (DMD) in patients with a confirmed specific genetic mutation. DMD is a rare, inherited muscle disease that is caused by absence ...

  9. Givinostat (Oral Route) Description and Brand Names - Mayo Clinic

    Givinostat is used to treat Duchenne muscular dystrophy (DMD). DMD is a rare, inherited muscle disease that is caused by the absence of a protein called ...

  10. Eteplirsen (Intravenous Route) Description and Brand Names - Mayo Clinic

    Eteplirsen injection is used to treat Duchenne muscular dystrophy (DMD) in patients with a confirmed mutation of the dystrophin gene amenable to exon 51 ...