Search Results 1-10 of 20236 for Duchenne+muscular+dystrophy

  1. Mayo Clinic Q and A: Understanding Duchenne muscular dystrophy

    ANSWER: As with all forms of muscular dystrophy, Duchenne muscular dystrophy is caused by a genetic defect. The defect leads to muscle weakness and loss of ...

  2. Muscular dystrophy - Symptoms & causes - Mayo Clinic

    Duchenne type muscular dystrophy · Frequent falls · Difficulty rising from a lying or sitting position · Trouble running and jumping · Waddling gait · Walking on the ...

  3. Muscular dystrophy - Diagnosis & treatment - Mayo Clinic

    In 2019, the Food and Drug Administration (FDA) approved golodirsen (Vyondys 53) for treatment of some people with Duchenne dystrophy who have a certain genetic ...

  4. Viltolarsen (Intravenous Route) Description and Brand Names - Mayo Clinic

    Viltolarsen injection is used to treat Duchenne muscular dystrophy (DMD) in patients with a confirmed specific genetic mutation. DMD is a rare, inherited muscle ...

  5. Muscular dystrophy - Doctors and departments - Mayo Clinic

    ... Duchenne muscular dystrophy, Degenerative disk disease, Cervical spondylotic myelopathy, Arthropathy, Inflammatory arthritis, Radiculopathy, Muscle weakness ...

  6. Delandistrogene Moxeparvovec-Rokl (Intravenous Route) Description and Brand Names - Mayo Clinic

    ... Duchenne muscular dystrophy (DMD) in patients with a confirmed specific genetic mutation. DMD is a rare, inherited muscle disease that is caused by absence ...

  7. Casimersen (Intravenous Route) Description and Brand Names - Mayo Clinic

    Casimersen injection is used to treat Duchenne muscular dystrophy (DMD) in patients with a confirmed specific genetic mutation. DMD is a rare, inherited muscle ...

  8. Eteplirsen (Intravenous Route) Description and Brand Names - Mayo Clinic

    Eteplirsen injection is used to treat Duchenne muscular dystrophy (DMD) in patients with a confirmed mutation of the dystrophin gene amenable to exon 51 ...

  9. Vamorolone (Oral Route) Description and Brand Names - Mayo Clinic

    Vamorolone is used to treat Duchenne muscular dystrophy (DMD). DMD is a rare, inherited muscle disease that is caused by absence of a protein called ...

  10. Deflazacort Expanded Access Program for Children, Adolescents and Adults With Duchenne Muscular Dystrophy - Mayo Clinic

    About this study. The expanded access program will provide access to treatment with deflazacort in children, adolescent, and adult patients with DMD in the ...