Drug information provided by: Merative, Micromedex®
Atidarsagene autotemcel injection is used to treat children with pre-symptomatic late infantile (PSLI), pre-symptomatic early juvenile (PSEJ), or early symptomatic early juvenile (ESEJ) metachromatic leukodystrophy (MLD).
Metachromatic leukodystrophy (MLD) is a rare genetic disorder that affects the brain and nervous system caused by a deficiency of an enzyme called arylsulfatase A (ARSA).
This medicine is to be given only by or under the immediate supervision of your doctor.
This product is available in the following dosage forms:
Portions of this document last updated: May 01, 2024
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