The possibilities of gene therapy hold much promise. Clinical trials of gene therapy in people have shown some success in treating certain diseases, such as:
- Severe combined immune deficiency
- Blindness caused by retinitis pigmentosa
But several significant barriers stand in the way of gene therapy becoming a reliable form of treatment, including:
- Finding a reliable way to get genetic material into cells
- Targeting the correct cells
- Reducing the risk of side effects
Gene therapy continues to be a very important and active area of research aimed at developing new, effective treatments for a variety of diseases.